Skip to content
RDA Rare Disease
Advocates
Menu

Neurology

  • Alzheimer’s Disease

    These advances underscore the importance of early diagnosis using biomarkers, including PET imaging and cerebrospinal fluid (CSF) analysis.

  • Amyotrophic Lateral Sclerosis (ALS)

    Amyotrophic Lateral Sclerosis (ALS) is a progressive motor neuron disease with limited treatment options historically. Recent breakthroughs include: Tofersen (Qalsody™) – antisense oligonucleotide for SOD1-mutated ALS On...

  • Migraine

    These therapies have significantly improved outcomes for patients with refractory or chronic migraine.

  • Multiple Sclerosis (MS)

    The goal of MS treatment has evolved toward early, high-efficacy therapy to preventirreversible disability.

  • Myasthenia Gravis (MG)

    These therapies allow for rapid symptom control while minimizing long-term immunosuppression.

  • Parkinson’s Disease

    Parkinson’s disease (PD) is a progressive neurodegenerative disorder characterized by the loss of dopaminergic neurons in the substantia nigra and the accumulation of alpha-synuclein aggregates (Lewy bodies). Clinically,...